10:00AM Case Study: Next-Generation AAVs for CNS Targeting: Enhancing Precision While Reducing Liver Tropism & Immunogenicity
Time: 10:00 am
day: Conference Day 1
Details:
• Exploring novel capsid modifications that improve blood-brain barrier crossing and increase therapeutic efficacy in neurological disorders
• Strategies to substantially detarget the liver, lowering systemic toxicity and reducing immune activation
• How advanced AAV engineering can mitigate immune responses, improve patient tolerability, and enhance long-term therapeutic success